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Stay updated with the latest news and developments from the ERAMET project. Discover how our groundbreaking work is transforming the development and approval processes for medicines targeting rare and pediatric diseases. Explore insights from our consortium and key milestones achieved along the way.

PRESS RELEASE: First-Year Achievements in Advancing Paediatric and Rare Disease Research

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YouTube Video VVVFcWhaUExnZW5PZU05UzVPQWR1M1JRLmtIYjRqbm5JUVVn In this clip from the BioMed21 webinar, Professor Francesco Pappalardo from the University of Catania introduces the EU-funded ERAMET Project and its mission to advance rare disease research using New Approach Methodologies (NAMs). Discover how ERAMET is building an integrated digital ecosystem, combining AI, computational models, and Human Digital Twins, in order to predict disease progression, personalise pediatric treatments, and pave a clear path toward regulatory acceptance for digital health technologies. 🔬👩‍🔬 Don't forget to like, subscribe, and stay tuned for more as we continue showcasing the people and innovations driving the ERAMET project. 🌐 Learn more about the project here: https://www.erametproject.eu
ERAMET Project 21
Francesco Pappalardo presentation of ERAMET at BioMed21
ERAMET Project July 9, 2026 1:29 pm
In this clip from the BioMed21 webinar, Professor Francesco Pappalardo from the University of Catania introduces the EU-funded ERAMET Project and its mission to advance rare disease research using New Approach Methodologies (NAMs). Discover how ERAMET is building an integrated digital ecosystem, combining AI, computational models, and Human Digital Twins, in order to predict disease progression, personalise pediatric treatments, and pave a clear path toward regulatory acceptance for digital health technologies. 🔬👩‍🔬 Don't forget to like, subscribe, and stay tuned for more as we continue showcasing the people and innovations driving the ERAMET project. 🌐 Learn more about the project here: https://www.erametproject.eu
Francesco Pappalardo presentation of ERAMET at BioMed21
YouTube Video VVVFcWhaUExnZW5PZU05UzVPQWR1M1JRLmtIYjRqbm5JUVVn
Welcome to a new episode of Meet the Consortium, our series introducing the researchers and professionals driving the ERAMET project. In this episode, we meet Donato Bonifazi, Chair of the TEDDY Network, the European Network of Excellence for Paediatric Clinical Research, which promotes collaboration and innovation to advance research for children across Europe. TEDDY Network Within ERAMET, Donato focuses on developing innovative methodologies to accelerate the development of medical products for small patient populations, where generating robust clinical evidence remains a major challenge. His work contributes to: * WP4: Clinical trial optimisation – designing more efficient and informative clinical trials. * WP5: Paediatric extrapolation – advancing approaches that responsibly use existing evidence to reduce unnecessary paediatric studies while ensuring safety and efficacy. * WP6: Predicting dose and treatment effects – developing predictive methods to optimise dosing strategies and improve treatment outcomes in small populations. 🔬👩‍🔬 Don't forget to like, subscribe, and stay tuned for more episodes as we continue showcasing the people and innovations driving the ERAMET project.
Meet the Consortium | Episode 8: Donato Bonifazi
YouTube Video VVVFcWhaUExnZW5PZU05UzVPQWR1M1JRLlRXUDUwYTBuVVRN
Welcome to a new episode of Meet the Consortium, a series in which we introduce the dedicated researchers and professionals behind the ERAMET project. In this episode, we meet Flora Musuamba from the University of Namur, the coordinator of ERAMET and the driving force behind the project. Flora holds a dual affiliation with UNamur and the Belgian Federal Agency, and her work primarily focuses on Work Packages 1, 2, and 7. The aim of her work, and of ERAMET as a whole, is to develop solutions that support both drug developers and assessors throughout the drug development and evaluation process, particularly in the fields of paediatric and rare diseases. ERAMET’s relevance also lies in the fact that the principles currently established are fully aligned with the most recent regulatory guidelines, such as ICH M15 and ICH E11A. Watch the full interview to know more! 🔬👩‍🔬 Don’t forget to like, subscribe, and stay tuned for more episodes as we continue exploring the impactful work taking place within ERAMET!
Meet the Consortium | Episode 7: Flora Musuamba – University of Namur
YouTube Video VVVFcWhaUExnZW5PZU05UzVPQWR1M1JRLkczMl95WTUwM09B
Welcome to Episode 6 of Meet the Consortium, the series where we introduce the brilliant minds behind the ERAMET project. In this episode, we meet Ine Skottheim Rusten, a founder and key researcher in Work Package 3 (WP3) of the ERAMET Project. Ine Skottheim Rusten is the founder of Systems Resource Lab AS (SRLAB), based in Norway. She is leading WP3 on the operationalisation of the Question-Centric approach for orphan and paediatric drug development and regulatory decision-making. Discover how WP3 is developing AI-based tools for data searching, extraction of relevant data and assessing its credibility for re-use in the specific context of developing and assessing the credibility of computational Modelling and Simulation methods. Practices for model development and credibility analysis are mapped, and techniques and tools for credibility assessment are gathered into a toolbox to prepare for automation and decision support as part of the ERAMET platform. A dedicated Digital Research Environment has been established to support real-world use cases, while ensuring sustainable, ethical and compliant data management. 🔬👩‍🔬 Don’t forget to like, subscribe, and stay tuned for more episodes as we continue to explore the impactful work happening within ERAMET!
Meet the Consortium | Episode 6: Ine Skottheim Rusten – Systems Resource Lab AS
YouTube Video VVVFcWhaUExnZW5PZU05UzVPQWR1M1JRLkdLM2FDU1RzSmFN
Welcome to Episode 5 of Meet the Consortium, the series where we introduce the brilliant minds behind the ERAMET project. In this episode, we meet Loes Maton, a key researcher in Work Package 2 (WP2) of the ERAMET project. Loes Maton is a PhD Candidate in Pharmacometrics at the University Medical Center of Groningen (UMCG) and Medicines Evaluation Board of College ter Beoordeling van Geneesmiddelen (CBG-MEB). She is part of the UMCG and CBG-MEB team leading WP2 on the use of modelling and simulation in paediatric study design. Discover how WP2 is trying to determine the ways that pharmaceutical companies calculate the amount of subjects that they need to include within their clinical studies. In order to investigate data that they obtain from those studies is sufficient for decision-making within the regulatory framework. 🔬👩‍🔬 Don’t forget to like, subscribe, and stay tuned for more episodes as we continue to explore the impactful work happening within ERAMET!
Meet the Consortium | Episode 5: Loes Maton – UMGC/CBG-MEB
YouTube Video VVVFcWhaUExnZW5PZU05UzVPQWR1M1JRLnI5cERTdDhob1JB
Welcome to Episode 4 of Meet the Consortium, the series where we introduce the brilliant minds behind the ERAMET project. In this episode, we meet Umberto Villani, a key researcher in Work Package 6 (WP6) of the ERAMET project. Umberto Villani is a biomedical engineer with a PhD in Neuroscience and a Postdoctoral Researcher in translational pharmacology at UCL. He is part of the UCL team leading WP6 on extrapolation in groups of rare diseases. Discover how WP6 is trying to pool knowledge on certain diseases to inform what is gonna happen with a certain medical product in another disease. 🔬👩‍🔬 Don’t forget to like, subscribe, and stay tuned for more episodes as we continue to explore the impactful work happening within ERAMET!
Meet the Consortium | Episode 4: Umberto Villani – UCL
YouTube Video VVVFcWhaUExnZW5PZU05UzVPQWR1M1JRLm13dUpNbVVIaGVZ
Welcome to Episode 3 of Meet the Consortium, the series where we introduce the brilliant minds behind the ERAMET project. In this episode, we meet Shalom Govere from the University of Namur, a key contributor to Work Package 2 (WP2). Shalom’s research focuses on sickle cell disease, a hemoglobinopathy, and aims to extract and structure regulatory questions from scientific advice documents. By analysing both industry and regulatory perspectives within these documents, Shalom helps build a richer, more comprehensive repository of regulatory insights. One of the core challenges she addresses is how to effectively structure this repository. Together with her WP2 colleagues, she has developed a structured and consistent methodology for data search, extraction, classification, and credibility assessment of regulatory questions. The team also uses a shared coding system to ensure consistency across disease areas and question types. Discover how WP2 is creating a solid regulatory framework to support the use of modelling and simulation, and meet the researchers shaping the future of innovative healthcare. 🔬👩‍🔬 Don’t forget to like, subscribe, and stay tuned for more episodes as we continue to explore the impactful work happening within ERAMET!
Meet the Consortium | Episode 3: Shalom Govere – University of Namur
YouTube Video VVVFcWhaUExnZW5PZU05UzVPQWR1M1JRLnYyTF9vYkpCUWFZ
Welcome to the second episode of Meet the Consortium, a series where we introduce the dedicated researchers and professionals behind the ERAMET project. In this episode, we meet Lisa Hanquet from the University of Namur, who plays a key role in Work Package 2 (WP2). Lisa’s work focuses on Advanced Therapeutic Medicinal Products (ATMPs), specifically CAR-T cell therapies — immune cells engineered to target and destroy tumour cells, mainly used today for blood cancers like multiple myeloma and acute lymphoblastic leukaemia. Lisa is building a repository of regulatory questions by analysing key documents such as the Public Assessment Report and the Electronic Common Technical Document (eCTD) submitted for marketing authorisation. Her work aims to integrate modelling and simulation into regulatory frameworks, identifying where these tools can support or enhance current assessments. She also plans to extend this approach to other regulatory documents like Paediatric Investigation Plans and scientific advice requests. Discover how WP2 is addressing complex regulatory challenges and meet the innovators driving ERAMET forward. 🔬👩‍🔬 Don’t forget to like, subscribe, and stay tuned for more episodes as we continue to explore the impactful work happening within ERAMET!
Meet the Consortium | Episode 2: Lisa Hanquet – University of Namur
YouTube Video VVVFcWhaUExnZW5PZU05UzVPQWR1M1JRLnFYUXdMWmVEcDVN
Welcome to the very first episode of Meet the Consortium, a series where we introduce the dedicated researchers and professionals behind the ERAMET project. In this episode, we meet Hélène Hauget from the University of Namur, who plays a key role in Work Package 2 (WP2). Hélène shares insights into her work, which focuses on pediatric asthma, and explains how her research contributes to the broader goals of the ERAMET consortium. Discover how WP2 is tackling complex health challenges, and learn more about the people driving innovation and collaboration across the project. 🔬👩‍🔬 Don’t forget to like, subscribe, and stay tuned for more episodes as we continue to explore the impactful work happening within ERAMET!
Meet the Consortium | Episode 1: Hélène Hauget – University of Namur
YouTube Video VVVFcWhaUExnZW5PZU05UzVPQWR1M1JRLndXRGo3cU01dW1j
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